Pfizer (PFE) stock gains as lung cancer therapy, Lorbrena, shows promising results in reducing disease progression or death ...
Pfizer is among companies working in recent years to develop DMD gene therapies. The first DMD gene therapy reached the market after Sarepta Therapeutics won FDA accelerated approval in June 2023 ...
Kendric Cromer is the first commercial patient to receive the groundbreaking treatment. Kendric Cromer, 12, is the first patient in the United States to undergo a newly approved gene therapy for ...
This health news summary spotlights major developments in cancer treatments, regulatory actions on biotechnology, and the ...
A top Food and Drug Administration official on Friday again advocated for the speedy approval of gene therapies for rare diseases. But he didn’t drop any clues on where the agency stands on a ...
the treatment of patients with paroxysmal nocturnal hemoglobinuria (PNH) to reduce hemolysis; and the treatment of patients with atypical hemolytic uremic syndrome (aHUS) to inhibit complement ...
A young boy died in a trial for Pfizer’s experimental gene therapy for Duchenne muscular dystrophy, the company told patient advocates Tuesday. The boy was enrolled in Daylight, a trial studying ...
The global cell and gene therapy market is experiencing significant growth, driven by technological advancements, increasing ...
Since the recombinant viral genomes are devoid of any viral genes (which are also not expressed by the infected target cell), the recombinant viral vectors can only infect a cell and are ...
Stimulants are typically the go-to option for doctors prescribing treatments for attention-deficit hyperactivity disorder (ADHD). But some ADHD patients do not respond adequately to stimulants or ...
When we think of smoking-related cancers, lung cancer usually comes to mind. But smoking is also a major driver for bladder cancer. Now, a new treatment has come to Philadelphia to help more ...
The drug is a potential treatment for biliary atresia in patients who have undergone surgery in which blocked bile ducts are bypassed to restore normal bile flow. The growth was driven by spending on ...